By Genetic Engineering & Biotechnology News –
According to at least one estimate, approximately 41,000 people in the United States have symptoms of Huntington’s disease, and more than 200,000 are at-risk of inheriting the disease. Symptoms of the neurodegenerative disorder, which is caused by a CAG expansion within exon 1 of the huntingtin gene, include personality changes, unsteady gait and involuntary movements, slurred speech, and more. Currently, there are multiple efforts underway to develop effective treatments, some of which are in clinical trials, that could slow or stop disease progression.
